ABC news story on gene therapy for teens going blind

A mutation in the RPE65 gene prevents normal vision. A revolutionary gene therapy treatment gives patients a normal copy of the RPE65 gene, restoring their sight. These Sydney siblings became the first people in Australia to receive this ground-breaking eye treatment.

Watch this ABC news story, that features our own Prof. Rasko.

Read more in the ABC news article.

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Ground-breaking gene therapy trial for haemophilia A

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New article by Power & Rasko in New Scientist on the stem cell revolution